Avlayah Approved for Neurologic Manifestations of Hunter Syndrome

Summary: The FDA just gave quick approval to a new medicine called Avlayah. It treats brain and nerve problems caused by Hunter syndrome, a rare disease mostly found in boys. Hunter syndrome happens when the body is missing a special enzyme, which causes harmful stuff to build up in the organs and the brain.

Avlayah works by replacing this missing enzyme. In a study with 47 kids, the medicine lowered the harmful buildup in their brain fluid by 91%. The medicine is given through an IV once a week. It can cause side effects like colds, fevers, and allergic reactions, so doctors must watch patients closely while they get it. It should be available in the US very soon!

For more details, see rssapp-neurologyadvisor-com at neurologyadvisor.com/news/avlayah-approved-for-neurologic-manifestations-of-hunter-syndrome/ (opens in new tab)